Severe PIs: Cutting-Edge Science Turns Tragedies to Cures

For decades, donor blood stem cell transplantation has been the only potential cure for severe primary immunodeficiency disorders, but it has been limited by failure and serious complication risks. Now, a trifecta of scientific advances is transforming the prognosis for children once defenseless against life-threatening infections.

Game On! The Age of Gamification

Healthcare industry stakeholders are increasingly using diagnosis-specific apps and educational gaming platforms to engage with patients, encourage compliance and even manage treatment options.

Long-Acting Factor Concentrates: The Next Leap Forward in Hemophilia Care Arrives

Treatment advances over the past 40 years have transformed the lives of people with hemophilia, and more innovation lies ahead.

21st Century Medicine: Now It’s Personal

Thanks to breakthroughs in genome sequencing, personalized medicine is rapidly becoming more science than fiction. As experimental therapies are replaced with data-driven solutions, we may be closer than ever to the kind of patient-specific care that promises to revolutionize the way medicine is practiced.

In the Pipeline: Novel Plasma Proteins for Major Cardiovascular Disorders

OVER THE 70 years since biochemist Edwin Cohn and his Harvard Medical School laboratory first purified human albumin for use in severe burns and hemorrhagic trauma, nearly 30 therapeutic proteins from human plasma have been purified, proven safe and effective and approved for use. Most of these products (Table 1) are indicated as replacement therapies […]

Tuberculosis Vaccine Effective as Treatment for MS

A recent study shows that a vaccine typically used to prevent tuberculosis in countries outside of the U.S. could also prevent multiple sclerosis (MS) in people who are in the beginning stages of the disease.

New Gene May Be an Effective Target for Autoimmune Disease Therapy

Researchers at King’s College London have identified a new gene, PIM1, which could be an effective target for innovative treatments and therapies for psoriasis, an autoimmune disease.

Immune System Therapy Shows Promise in Adults with Leukemia

A recent study of an experimental therapy that alters cancer patients’ own immune cells to recognize an often deadly form of leukemia has shrunk tumors and sent the cancer into remission in adults.

Immune Globulin: Each Product Is Unique

While all IG products are comparably effective, they also have relevant differences that determine their tolerability by patients.

A Review of Coagulation Factor Disorders

Until better treatments or a cure can be found, coagulation factor replacement therapies continue to improve the long-term outcome for people with bleeding disorders